FDA approval of LAD gene therapy
Last Thursday, the FDA approved the LAD gene therapy developed by Juan A. Bueren and Elena Almarza, in collaboration with the Adrian Thrasher team. This treatment was licensed to Rocket Pharma, who developed the clinical trial and presented it to the FDA. We believe this is terrific news for the gene therapy field and for SETGYC, as a lot of these advances have come from SETGYC members, and the society has played a fundamental role in favouring this collaboration and in the d
En memoria del Dr Ernest Arenas Cases (1962 – 2024)
El “Professor” Ernest Arenas nos ha dejado de forma prematura e inesperada. Brillante neurocientífico y excelente persona. Una vida dedicada a la ciencia, abordando uno de los principales retos médicos de nuestra sociedad: la búsqueda de tratamientos para las enfermedades neurodegenerativas. El Dr Arenas nació en 1962 en Lleida, aunque pasó su infancia en Manresa. Estudió Medicina y Cirugía en la Universidad de Lleida. Posteriormente realizó su tesis doctoral en la Universida
Fondazione Telethon announces submission of MAA to EMA for Gene Therapy for the treatment of Wiskott-Aldrich Syndrome patients
Read the press release here for full details.
