FDA approval of LAD gene therapy

Last Thursday, the FDA approved the LAD gene therapy developed by Juan A. Bueren and Elena Almarza, in collaboration with the Adrian Thrasher team. This treatment was licensed to Rocket Pharma, who developed the clinical trial and presented it to the FDA. We believe this is terrific news for the gene therapy field and for SETGYC, as a lot of these advances have come from SETGYC members, and the society has played a fundamental role in favouring this collaboration and in the development of all those gene therapy approaches.

More information available on this press release

And in this article published in EL MUNDO.