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Wednesday 1 June
Room: Descubrimiento
12:30-13:30
Plenary 8: in vivo Gene editing applications
Chairs: Gloria Aseguinolaza, University of Navarra, Pamplona; Juan Bueren, CIEMAT, Madrid
12:30 Gloria Gonzalez Aseguinolaza, University of Navarra, Pamplona ⓘ
INV53 In vivo gene editing to treat Primary hyperoxaluria type I
13:00 Jordi Barquinero, Vall d'Hebron Research Institute, Barcelona ⓘ
INV54 In vivo gene editing for Mitochondrial NeuroGastroIntestinal Encephalomyopathy
13:30 Ignacio Perez de Castro, Instituto de Salud Carlos III, Madrid
OR22 CRISPR-based strategies revert the LMNAᴿ²⁴⁹ᵂ induced phenotype both in cultured cells and in vivo
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